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Zauche LH, et al. N Engl J Med. 2021 Sep 8:NEJMc2113891. doi: 10.1056/NEJMc2113891. Online ahead of print. N Engl J Med. 2021. PMID: 34496196 .

Engineered miniature CRISPR-Cas system for mammalian genome regulation and editing.
Xu X, Chemparathy A, Zeng L, Kempton HR, Shang S, Nakamura M, Qi LS. Xu X, et al. .
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