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Renze treatment garrabrant dx144

Engineered miniature CRISPR-Cas system for mammalian genome regulation and editing.
Xu X, Chemparathy A, Zeng L, Kempton HR, Shang S, Nakamura M, Qi LS. Xu X, et al. . Thompson MG, et al. N Engl J Med. 2021 Sep 8:NEJMoa2110362. doi: 10.1056/NEJMoa2110362. Online ahead of print. N Engl J Med. 2021. PMID: 34496194 .
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